Gene Therapies

• A Method of Genetically Modifying Human Hematopoietic Stem Cells MK+10-009-A-Method-of-Genetically-Modifying-Human-Hematopoietic-Stem-Cells
• Adeno-Associated Virus Mediated Delivery of Genes to Pancreatic Beta-Cells for Improved Efficacy of Transplantation MK+10-006-Adeno-Associated-Virus-Mediated-Delivery-of-Genes-to-Pancreatic-Beta-Cells-for-Improved-Efficacy-of-Transplantation
• Lentiviral Vector for Site-Specific Gene Integration MK+10-012-Lentiviral-Vector-for-Site-Specific-Gene-Integration
• Novel AAV Vectors Optimized for Therapeutic Gene Transfer MK+10-019-Novel-AAV-Vectors-Optimized-for-Therapeutic-Gene-Transfer
• Regulating Cells through Synthetic RNA Switch Control systems MK+12-092-Regulating-Cells-through-Synthetic-RNA-Switch-Control-systems
• Ribozymes Targeted to Human CCR5 mRNA for Treatment of HIV MK+12-101-Ribozymes-Targeted-to-Human-CCR5-mRNA-for-Treatment-of-HIV
• Site-Specific Integration ofrep-deleted rAAV MK+10-010-Site-Specific-Integration-ofrep-deleted-rAAV
• Treatment for Metastatic Melanoma Utilizing a Targeted Killer Gene MK+10-014-Treatment-for-Metastatic-Melanoma-Utilizing-a-Targeted-Killer-Gene